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2019 MDA Abstract – NSAA Shift Analyses

2019 MDA Abstract – NSAA Shift Analyses

One-year shifts in North Star Ambulatory Assessment items in Duchene muscular dystrophy (DMD) patients in the UK NorthStar Network database

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13
Apr 2019
Abstracts

Read the latest

  • Prognostic factors for loss of ability to rise from supine in DMD
  • Suitability of external controls for drug evaluation in Duchenne muscular dystrophy
  • cTAP Study Shows Real-World, Natural History Data Comparable to Placebo Data from Clinical Trials in Duchenne Muscular Dystrophy
  • A prognostic model for 1 year change in 4SC
  • Deflazacort vs prednisone treatment for Duchenne muscular dystrophy

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