Suitability of external controls for drug evaluation in Duchenne muscular dystrophy

Suitability of external controls for drug evaluation in Duchenne muscular dystrophy
Nathalie Goemans, James Signorovitch, Gautam Sajeev, Zhiwen Yao, Heather Gordish-Dressman, Craig M. McDonald, Krista Vandenborne, Debra Miller, Susan J. Ward, Eugenio Mercuri, for the investigators from PRO-DMD-01 Study, CINRG DNHS, ImagingDMD, and the DMD Italian Group