AllAbstractsNews & PressPresentationsPublications Read More Prognostic factors for loss of ability to rise from supine in DMD 2020 Read More Suitability of external controls for drug evaluation in Duchenne muscular dystrophy 2020 Read More cTAP Study Shows Real-World, Natural History Data Comparable to Placebo Data from Clinical Trials in Duchenne Muscular Dystrophy 2020 Read More A prognostic model for 1 year change in 4SC 2020 Read More Deflazacort vs prednisone treatment for Duchenne muscular dystrophy 2020 Read More Real-world outcomes of long-term prednisone and deflazacort use in patients with Duchenne muscular dystrophy 2020 Read More Nature Biotechnology: Their Lives in Their Hands 2019 Read More cTAP Publishes Comprehensive Analysis of NSAA 2019 Read More Categorising trajectories and individual item changes of the NSAA in patients with DMD 2019 Read More 2019 EAN Abstract - Phase 1b/2 Study of RG6206 2019 Read More cTAP Abstract for 2019 NORD Summit 2019 Read More 2019 EU ISPOR Abstract - NSAA consistency analysis 2019 Read More 2019 EU ISPOR Abstract - Prognostic Model for Loss of Walking in DMD 2019 Read More 2019 JSCN Abstract - Phase 1b/2 Study of RG6206 2019 Read More 2019 MDA Abstract - NSAA Shift Analyses 2019 Read More 2019 MDA Abstract - The Collaborative Trajectory Analysis Project (cTAP) 2019 Read More 2019 PTC WMS Abstract - Steroid Use and DMD 2019 Read More 2019 WMS Abstract - Prognostic score for loss of walking ability in DMD 2019 Read More 2019 WMS Abstract - 48-Week Changes in NSAA 2019 Read More 2019 WMS Abstract - Lean Body Mass and Motor Function in DMD Patients 2019 Read More 2019 WMS Abstract - Estimating Changes in NSAA and 4SC in DMD 2019 Read More 2019 Myology Abstract - Changes in 4SC over Two Years in DMD 2019 Read More cTAP Partner Wins ISPOR Award on Duchenne Muscular Dystrophy 2018 Read More cTAP at the 2018 Action Duchenne Conference 2018 Read More 2018 ISPOR EU Abstract - Ambulatory Function in Duchenne Muscular Dystrophy 2018 Read More Moneyball Medicine: Thriving in the new data-driven healthcare market 2018 Read More 2018 Action Duchenne abstract - Longitudinal analyses of 4SC velocity in Leuven 2018 Read More WMS 2018 Abstract - Consistency of 6MWD 2018 Read More WMS 2018 Abstract - Minimal detectable change in NSAA 2018 Read More WMS 2018 Abstract - 4SC Velocity Prognostic Model 2018 Read More cTAP to Present Late-breaking Results at the World Muscle Society Congress 2018 Read More cTAP Presentation at the 2018 ASA Biopharmaceutical Section Regulatory-Industry Statistics Workshop 2018 Read More 2018 Action Duchenne abstract - Consistency of 1-year change in 6MWD 2018 Read More Action Duchenne International Conference 2018 Abstract - Phase 1b/2 study of the anti-myostatin adnectin RG6206 2018 Read More 2018 Action Duchenne abstract - MCID of 4SC and NSAA in CCHMC 2018 Read More 2018 ICNMD - 4SC prognostic model 2018 Read More cTAP to Present at Annual Biopharmaceutical Conference 2018 Read More cTAP at the 2018 ISPOR Conference 2018 Read More 2017 WMS Abstract - Validation of a prognostic score for changes in 6MWD 2017 Read More 2017 WMS Abstract - The Collaborative Trajectory Analysis Collaboration 2017 Read More 2017 WMS Abstract - Consistency between natural history and clinical trial placebo 2017 Read More 2017 WMS Abstract - Clustering Trajectories of Ambulatory Function 2017 Read More Summit Therapeutics Joins cTAP to Support the Development of Potential DMD Treatments 2017 Read More R&D Partnerships 2017 Read More Modern Solutions to Recurring Roadblocks in Clinical Testing 2017 Read More cTAP at the 2017 IRDiRC Conference 2017 Read More Marathon Pharmaceuticals and Italfarmaco Join cTAP 2017 Read More 2017 IRDiRC Abstract - Translating Natural History into Clinical Trial Design 2017 Read More Eli Lilly and Company Joins cTAP 2016 Read More Nontraditional Approaches to Big Data Analyses: A Case Study in Rare Disease 2016 Read More cTAP Announces Two Research Publications 2016 Read More Non-Profits, Pharmaceutical Companies and Noted Clinicians Collaborate to Launch cTAP 2016 Read More Individualized Prediction of Changes in 6-Minute Walk Distance for Patients with Duchenne Muscular Dystrophy 2016 Read More Supplemental Materials on Neuromuscular Disorders 2016 Read More Categorizing natural history trajectories of ambulatory function 2016 Read More cTAP at the TREAT-NMD 2015 Conference 2015 Read More cTAP at the World Congress Orphan Disease Conference 2015 2015 Read More cTAP at the 2015 PPMD Conference 2015
AllAbstractsNews & PressPresentationsPublications Read More Prognostic factors for loss of ability to rise from supine in DMD 2020 Read More Suitability of external controls for drug evaluation in Duchenne muscular dystrophy 2020 Read More cTAP Study Shows Real-World, Natural History Data Comparable to Placebo Data from Clinical Trials in Duchenne Muscular Dystrophy 2020 Read More A prognostic model for 1 year change in 4SC 2020 Read More Deflazacort vs prednisone treatment for Duchenne muscular dystrophy 2020 Read More Real-world outcomes of long-term prednisone and deflazacort use in patients with Duchenne muscular dystrophy 2020 Read More Nature Biotechnology: Their Lives in Their Hands 2019 Read More cTAP Publishes Comprehensive Analysis of NSAA 2019 Read More Categorising trajectories and individual item changes of the NSAA in patients with DMD 2019 Read More 2019 EAN Abstract - Phase 1b/2 Study of RG6206 2019 Read More cTAP Abstract for 2019 NORD Summit 2019 Read More 2019 EU ISPOR Abstract - NSAA consistency analysis 2019 Read More 2019 EU ISPOR Abstract - Prognostic Model for Loss of Walking in DMD 2019 Read More 2019 JSCN Abstract - Phase 1b/2 Study of RG6206 2019 Read More 2019 MDA Abstract - NSAA Shift Analyses 2019 Read More 2019 MDA Abstract - The Collaborative Trajectory Analysis Project (cTAP) 2019 Read More 2019 PTC WMS Abstract - Steroid Use and DMD 2019 Read More 2019 WMS Abstract - Prognostic score for loss of walking ability in DMD 2019 Read More 2019 WMS Abstract - 48-Week Changes in NSAA 2019 Read More 2019 WMS Abstract - Lean Body Mass and Motor Function in DMD Patients 2019 Read More 2019 WMS Abstract - Estimating Changes in NSAA and 4SC in DMD 2019 Read More 2019 Myology Abstract - Changes in 4SC over Two Years in DMD 2019 Read More cTAP Partner Wins ISPOR Award on Duchenne Muscular Dystrophy 2018 Read More cTAP at the 2018 Action Duchenne Conference 2018 Read More 2018 ISPOR EU Abstract - Ambulatory Function in Duchenne Muscular Dystrophy 2018 Read More Moneyball Medicine: Thriving in the new data-driven healthcare market 2018 Read More 2018 Action Duchenne abstract - Longitudinal analyses of 4SC velocity in Leuven 2018 Read More WMS 2018 Abstract - Consistency of 6MWD 2018 Read More WMS 2018 Abstract - Minimal detectable change in NSAA 2018 Read More WMS 2018 Abstract - 4SC Velocity Prognostic Model 2018 Read More cTAP to Present Late-breaking Results at the World Muscle Society Congress 2018 Read More cTAP Presentation at the 2018 ASA Biopharmaceutical Section Regulatory-Industry Statistics Workshop 2018 Read More 2018 Action Duchenne abstract - Consistency of 1-year change in 6MWD 2018 Read More Action Duchenne International Conference 2018 Abstract - Phase 1b/2 study of the anti-myostatin adnectin RG6206 2018 Read More 2018 Action Duchenne abstract - MCID of 4SC and NSAA in CCHMC 2018 Read More 2018 ICNMD - 4SC prognostic model 2018 Read More cTAP to Present at Annual Biopharmaceutical Conference 2018 Read More cTAP at the 2018 ISPOR Conference 2018 Read More 2017 WMS Abstract - Validation of a prognostic score for changes in 6MWD 2017 Read More 2017 WMS Abstract - The Collaborative Trajectory Analysis Collaboration 2017 Read More 2017 WMS Abstract - Consistency between natural history and clinical trial placebo 2017 Read More 2017 WMS Abstract - Clustering Trajectories of Ambulatory Function 2017 Read More Summit Therapeutics Joins cTAP to Support the Development of Potential DMD Treatments 2017 Read More R&D Partnerships 2017 Read More Modern Solutions to Recurring Roadblocks in Clinical Testing 2017 Read More cTAP at the 2017 IRDiRC Conference 2017 Read More Marathon Pharmaceuticals and Italfarmaco Join cTAP 2017 Read More 2017 IRDiRC Abstract - Translating Natural History into Clinical Trial Design 2017 Read More Eli Lilly and Company Joins cTAP 2016 Read More Nontraditional Approaches to Big Data Analyses: A Case Study in Rare Disease 2016 Read More cTAP Announces Two Research Publications 2016 Read More Non-Profits, Pharmaceutical Companies and Noted Clinicians Collaborate to Launch cTAP 2016 Read More Individualized Prediction of Changes in 6-Minute Walk Distance for Patients with Duchenne Muscular Dystrophy 2016 Read More Supplemental Materials on Neuromuscular Disorders 2016 Read More Categorizing natural history trajectories of ambulatory function 2016 Read More cTAP at the TREAT-NMD 2015 Conference 2015 Read More cTAP at the World Congress Orphan Disease Conference 2015 2015 Read More cTAP at the 2015 PPMD Conference 2015
